Publications

An endogenous peptide marker differentiates SOD1 stability and facilitates pharmacodynamic monitoring in SOD1 amyotrophic lateral sclerosis

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Gertsman, I., Wuu, J., McAlonis-Downes, M., (…), *Miller, T.M., Da Cruz, S., JCI Insight, Volume 4, Issue 10, 2019, Article number e122768, 2019.