Suzuki-Hatano, S., Saha, M., Rizzo, S.A., (…), *Cade, W.T., Pacak, C.A. Human Gene Therapy, 30(2), pp. 139-154, 2019.
AAV-Mediated TAZ Gene Replacement Restores Mitochondrial and Cardioskeletal Function in Barth Syndrome
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Suzuki-Hatano, S., Saha, M., Rizzo, S.A., (…), *Cade, W.T., Pacak, C.A. Human Gene Therapy, 30(2), pp. 139-154, 2019.